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Genetics and its uses in Healthcare

##article.authors##

  • Kayal Balaji polygence

DOI:

https://doi.org/10.58445/rars.2367

Abstract

Advances in genetics and gene editing have affected future healthcare in many revolutionary ways. CRISPR-Cas9 is one of the most significant technologies to treat autosomal dominant disorders by preventing possible harmful diseases and alleles. Gene editing is a type of effective gene therapy that has had promising effects as well as a lot more to discover. Clinical trials are needed to evaluate the safety, effectiveness, and side effect concerns of new therapies.

References

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Medline plus. “Sickle Cell Disease.” Medlineplus.gov, National Library of Medicine, 25

Nov. 2020, medlineplus.gov/sicklecelldisease.html.

Mengstie, Misganaw Asmamaw, and Belay Zawdie Wondimu. “Mechanism and Applications of CRISPR/Cas-9-Mediated Genome Editing.” Biologics, vol. Volume 15, Aug. 2021, pp. 353–61. https://doi.org/10.2147/btt.s326422.

TREAT-NMD. “Gene Therapy for DMD - TREAT-NMD.” TREAT-NMD, 4 Dec. 2024,

www.treat-nmd.org/resources-and-support/research-overview/dmd/gene-therapy.

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Posted

2025-03-24

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